Research

Scientific publications

  • Schlüter, A, Vélez-Santamaría, V, Verdura, E, Rodríguez-Palmero, A, Ruiz, M, Fourcade, S, Planas-Serra, L, Launay, N, Guilera, C, Martínez, JJ, Homedes-Pedret, C, Albertí-Aguiló, MA, Zulaika, M, Marti, I, Troncoso, M, Tomás-Vila, M, Bullich, G, García-Pérez, MA, Sobrido-Gómez, MJ, López-Laso, E, Fons, C, Del Toro, M, Macaya, A, Beltran, S, Gutiérrez-Solana, LG, Pérez-Jurado, LA, Aguilera-Albesa, S, de Munain, AL, Casasnovas, C, Pujol, A and HSP Ataxia Workgrp.

    ClinPrior: an algorithm for diagnosis and novel gene discovery by network-based prioritization

    Genome Medicine 15(1):

    [doi:10.1186/s13073-023-01214-2]

  • Martinez-Piñeiro, A, Lucente, G, Hernandez-Perez, M, Cortés, J, Arbex, A, de la Ossa, NP, Ramos-Fransí, A, Almendrote, M, Millán, M, Gomis, M, Dorado, L, Castaño, C, Remollo, S, Cuadras, P, Garrido, A, Guanyabens, N, Broto, J, López-Cancio, E, Coll-Canti, J and Dávalos, A.

    Prognostic Accuracy of N20 Somatosensory Potential in Patients With Acute Ischemic Stroke and Endovascular Thrombectomy

    Stroke-Vascular And Interventional Neurology 3(5):

    [doi:10.1161/SVIN.122.000735]

  • Launay, N, Ruiz, M, Planas-Serra, L, Verdura, E, Rodríguez-Palmero, A, Schlüter, A, Goicoechea, L, Guilera, C, Casas, J, Campelo, F, Jouanguy, E, Casanova, JL, Boespflug-Tanguy, O, Cancela, MV, Gutiérrez-Solana, LG, Casasnovas, C, Area-Gomez, E and Pujol, A.

    RINT1 deficiency disrupts lipid metabolism and underlies a complex hereditary spastic paraplegia

    Journal of Clinical Investigation 133(14):

    [doi:10.1172/JCI162836]

  • Rovira-Remisa, MM, Moreira, M, Ventura, PS, Gonzalez-Alvarez, P, Mestres, N, Torres, FG, Joaquín, C, Seuma, ARP, Martínez-Colls, MD, Roche, A, Ibáñez-Micó, S, López-Laso, E, Méndez-Hernández, MJ, Murillo, M, Monlleó-Neila, L, Maqueda-Castellote, E, Riera, MD, Felipe-Rucían, A, Giralt-López, M and Cortès-Saladelafont, E.

    Impact of COVID19 pandemic on patients with rare diseases in Spain, with a special focus on inherited metabolic diseases

    Molecular Genetics and Metabolism Reports 35:

    [doi:10.1016/j.ymgmr.2023.100962]

  • Cortes-Saladelafont, E, Fernandez-Martin, J and Ortolano, S.

    Fabry Disease and Central Nervous System Involvement: From Big to Small, from Brain to Synapse

    International Journal of Molecular Sciences 24(6):

    [doi:10.3390/ijms24065246]

  • Mutze, U, Gleich, F, Baric, I, Baumgartner, M, Burlina, A, Chapman, KA, Chien, YH, Cortes-Saladelafont, E, De Laet, C, Dobbelaere, D, Eysken, F, Gautschi, M, Santer, R, Haberle, J, Joaquin, C, Karall, D, Lindner, M, Lund, AM, Muhlhausen, C, Murphy, E, Roland, D, Gomez, AR, Skouma, A, Grunert, SC, Wagenmakers, M, Garbade, SF, Kolker, S and Boy, N.

    Impact of the SARS-CoV-2 pandemic on the health of individuals with intoxication-type metabolic diseases-Data from the E-IMD consortium

    Journal of Inherited Metabolic Disease 46(2): 220-231

    [doi:10.1002/jimd.12572]

  • Villarreal-Salazar, M., Santalla, A., Real-Martinez, A., Nogales-Gadea, G., Valenzuela, P. L., Fiuza-Luces, C., Andreu, A. L., Rodriguez-Aguilera, J. C., Martin, M. A., Arenas, J., Vissing, J., Lucia, A., Krag, T. O. and Pinos, T..

    Low aerobic capacity in McArdle disease: A role for mitochondrial network impairment?

    Molecular Metabolism 66:

    [doi:10.1016/j.molmet.2022.101648]

  • Verdura, E, Senger, B, Raspall-Chaure, M, Schluter, A, Launay, N, Ruiz, M, Casasnovas, C, Rodriguez-Palmero, A, Macaya, A, Becker, HD and Pujol, A.

    Loss of seryl-tRNA synthetase (SARS1) causes complex spastic paraplegia and cellular senescence

    Journal of Medical Genetics 59(12): 1227-1233

    [doi:10.1136/jmg-2022-108529]

  • Alfonsi, C, Stephan-Otto, C, Cortes-Saladelafont, E, Palacios, NJ, Podzamczer-Valls, I, Cruz, NG, Jimenez, MRD, Mico, SI, Vila, MT, Jeltsch, K, Hubschmann, OK, Opladen, T, Fragua, RV, Gomez, T, Fortuny, OA, Jimenez, IG, Laso, EL, Martinez, AR, Lopez, JM and Garcia-Cazorla, A.

    Volumetric study of brain MRI in a cohort of patients with neurotransmitter disorders

    Neuroradiology 64(11): 2179-2190

    [doi:10.1007/s00234-022-02989-8]

  • Garcia-Puga, M, Saenz-Antonanzas, A, Gerenu, G, Arrieta-Legorburu, A, Fernandez-Torron, R, Zulaica, M, Saenz, A, Elizazu, J, Nogales-Gadea, G, Gadalla, SM, Arauzo-Bravo, MJ, de Munain, AL and Matheu, A.

    Senescence plays a role in myotonic dystrophy type 1 br

    JCI insight 7(19):

    [doi:10.1172/jci.insight.159357]

  • Hubschmann, OK, Julia-Palacios, NA, Olivella, M, Guder, P, Zafeiriou, DI, Horvath, G, Kulhanek, J, Pearson, TS, Kuster, A, Cortes-Saladelafont, E, Ibanez, S, Garcia-Jimenez, MC, Honzik, T, Santer, R, Jeltsch, K, Garbade, SF, Hoffmann, GF, Opladen, T and Garcia-Cazorla, A.

    Integrative Approach to Predict Severity in Nonketotic Hyperglycinemia

    Annals of Neurology 92(2): 292-303

    [doi:10.1002/ana.26423]

  • Davalos, V, Garcia-Prieto, CA, Ferrer, G, Aguilera-Albesa, S, Valencia-Ramos, J, Rodriguez-Palmero, A, Ruiz, M, Planas-Serra, L, Jordan, I, Alegria, I, Flores-Perez, P, Cantarin, V, Fumado, V, Viadero, MT, Rodrigo, C, Mendez-Hernandez, M, Lopez-Granados, E, Colobran, R, Riviere, JG, Soler-Palacin, P, Pujol, A and Esteller, M.

    Epigenetic profiling linked to multisystem inflammatory syndrome in children (MIS-C): A multicenter, retrospective study

    EClinicalMedicine 50:

    [doi:10.1016/j.eclinm.2022.101515]

  • Santalla, A, Valenzuela, PL, Rodriguez-Lopez, C, Rodriguez-Gomez, I, Nogales-Gadea, G, Pinos, T, Arenas, J, Martin, MA, Santos-Lozano, A, Moran, M, Fiuza-Luces, C, Ara, I and Lucia, A.

    Long-Term Exercise Intervention in Patients with McArdle Disease: Clinical and Aerobic Fitness Benefits

    MEDICINE & SCIENCE IN SPORTS & EXERCISE 54(8): 1231-1241

    [doi:10.1249/MSS.0000000000002915]

  • Julia-Palacios, N, Molina-Anguita, C, Bondarenko, MS, Cortes-Saladelafont, E, Aparicio, J, Cuadras, D, Horvath, G, Fons, C, Artuch, R and Garcia-Cazorla, A.

    Monoamine neurotransmitters in early epileptic encephalopathies: New insights into pathophysiology and therapy

    Developmental Medicine and Child Neurology 64(7): 915-923

    [doi:10.1111/dmcn.15140]

  • Koehorst, E, Odria, R, Capo, J, Nunez-Manchon, J, Arbex, A, Almendrote, M, Linares-Pardo, I, Natera-de Benito, D, Saez, V, Nascimento, A, Ortez, C, Rubio, MA, Diaz-Manera, J, Alonso-Perez, J, Lucente, G, Rodriguez-Palmero, A, Ramos-Fransi, A, Martinez-Pineiro, A, Nogales-Gadea, G and Suelves, M.

    An Integrative Analysis of DNA Methylation Pattern in Myotonic Dystrophy Type 1 Samples Reveals a Distinct DNA Methylation Profile between Tissues and a Novel Muscle-Associated Epigenetic Dysregulation

    Biomedicines 10(6):

    [doi:10.3390/biomedicines10061372]

  • Garcia-Consuegra, I, Asensio-Pena, S, Garrido-Moraga, R, Pinos, T, Dominguez-Gonzalez, C, Santalla, A, Nogales-Gadea, G, Serrano-Lorenzo, P, Andreu, AL, Arenas, J, Zugaza, JL, Lucia, A and Martin, MA.

    Identification of Potential Muscle Biomarkers in McArdle Disease: Insights from Muscle Proteome Analysis

    International Journal of Molecular Sciences 23(9):

    [doi:10.3390/ijms23094650]

  • Nunez-Alvarez, Y and Suelves, M.

    HDAC11: a multifaceted histone deacetylase with proficient fatty deacylase activity and its roles in physiological processes

    FEBS Journal 289(10): 2771-2792

    [doi:10.1111/febs.15895]

  • Corral-Juan, M, Casquero, P, Giraldo-Restrepo, N, Laurie, S, Martinez-Pineiro, A, Mateo-Montero, RC, Ispierto, L, Vilas, D, Tolosa, E, Volpini, V, Alvarez-Ramo, R, Sanchez, I and Matilla-Duenas, A.

    New spinocerebellar ataxia subtype caused by SAMD9L mutation triggering mitochondrial dysregulation (SCA49)

    Brain Communications 4(2):

    [doi:10.1093/braincomms/fcac030]

  • Schluter, A, Rodriguez-Palmero, A, Verdura, E, Velez-Santamaria, V, Ruiz, M, Fourcade, S, Planas-Serra, L, Martinez, JJ, Guilera, C, Giros, M, Artuch, R, Yoldi, ME, O'Callaghan, M, Garcia-Cazorla, A, Armstrong, J, Marti, I, Rezola, EM, Redin, C, Mandel, JL, Conejo, D, Sierra-Corcoles, C, Beltran, S, Gut, M, Vazquez, E, Del Toro, M, Troncoso, M, Perez-Jurado, LA, Gutierrez-Solana, LG, de Munain, AL, Casasnovas, C, Aguilera-Albesa, S, Macaya, A and Pujol, A.

    Diagnosis of Genetic White Matter Disorders by Singleton Whole-Exome and Genome Sequencing Using Interactome-Driven Prioritization

    Neurology 98(9): 912-923

    [doi:10.1212/WNL.0000000000013278]

  • Panciroli, C, Esteve, A, Munoz-Ferrer, A, Abad, J, Hernandez, JM, Balana, C, Lucente, G, Comas, S and Villa, S.

    Prospective pilot study to explore the melatonin level in brain tumor patients undergoing radiotherapy

    Sleep and Breathing 26(1): 469-475

    [doi:10.1007/s11325-021-02365-5]

  • Martin-Aguilar, L, Lleixa, C, Pascual-Goni, E, Caballero-Avila, M, Martinez-Martinez, L, Diaz-Manera, J, Rojas-Garcia, R, Cortes-Vicente, E, Turon-Sans, J, de Luna, N, Suarez-Calvet, X, Gallardo, E, Rajabally, Y, Scotton, S, Jacobs, BC, Baars, A, Cortese, A, Vegezzi, E, Hoftberger, R, Zimprich, F, Roesler, C, Nobile-Orazio, E, Liberatore, G, Hiew, FL, Martinez-Pineiro, A, Carvajal, A, Pinar-Morales, R, Uson-Martin, M, Alberti, O, Lopez-Perez, MA, Marquez, F, Pardo-Fernandez, J, Munoz-Delgado, L, Cabrera-Serrano, M, Ortiz, N, Bartolome, M, Duman, O, Bril, V, Segura-Chavez, D, Pitarokoili, K, Steen, C, Illa, I and Querol, L.

    Clinical and Laboratory Features in Anti-NF155 Autoimmune Nodopathy

    Neurology-Neuroimmunology & Neuroinflammation 9(1):

    [doi:10.1212/NXI.0000000000001098]

  • Villarreal-Salazar, M, Brull, A, Nogales-Gadea, G, Andreu, AL, Martin, MA, Arenas, J, Santalla, A, Lucia, A, Vissing, J, Krag, TO and Pinos, T.

    Preclinical Research in McArdle Disease: A Review of Research Models and Therapeutic Strategies

    Genes 13(1):

    [doi:10.3390/genes13010074]

  • Kumru, H, Albu, S, Oguz, S, Murillo, N, Lucente, G and Valls-Sole, J.

    Effects of different vibration frequencies on spinal cord reflex circuits and thermoalgesic perception

    JOURNAL OF MUSCULOSKELETAL & NEURONAL INTERACTIONS 21(4): 533-541

  • Koehorst, E, Nunez-Manchon, J, Ballester-Lopez, A, Almendrote, M, Lucente, G, Arbex, A, Chojnacki, J, Vazquez-Manrique, RP, Gomez-Escribano, AP, Pintos-Morell, G, Coll-Canti, J, Ramos-Fransi, A, Martinez-Pineiro, A, Suelves, M and Nogales-Gadea, G.

    Characterization of RAN Translation and Antisense Transcription in Primary Cell Cultures of Patients with Myotonic Dystrophy Type 1

    Journal of Clinical Medicine 10(23):

    [doi:10.3390/jcm10235520]

  • Wilson, MP, Garanto, A, Vairo, FPE, Ng, BG, Ranatunga, WK, Ventouratou, M, Baerenfaenger, M, Huijben, K, Thiel, C, Ashikov, A, Keldermans, L, Souche, E, Vuillaumier-Barrot, S, Dupre, T, Michelakakis, H, Fiumara, A, Pitt, J, White, SM, Lim, SC, Gallacher, L, Peters, H, Rymen, D, Witters, P, Ribes, A, Morales-Romero, B, Rodriguez-Palmero, A, Ballhausen, D, de Lonlay, P, Barone, R, Janssen, MCH, Jaeken, J, Freeze, HH, Matthijs, G, Morava, E and Lefeber, DJ.

    Active site variants in STT3A cause a dominant type I congenital disorder of glycosylation with neuromusculoskeletal findings

    American Journal of Human Genetics 108(11): 2130-2144

    [doi:10.1016/j.ajhg.2021.09.012]

  • Hochberg, I, Demain, LAM, Richer, J, Thompson, K, Urquhart, JE, Rea, A, Pagarkar, W, Rodriguez-Palmero, A, Schluter, A, Verdura, E, Pujol, A, Quijada-Fraile, P, Amberger, A, Deutschmann, AJ, Demetz, S, Gillespie, M, Belyantseva, IA, McMillan, HJ, Barzik, M, Beaman, GM, Motha, R, Ng, KY, O'Sullivan, J, Williams, SG, Bhaskar, SS, Lawrence, IR, Jenkinson, EM, Zambonin, JL, Blumenfeld, Z, Yalonetsky, S, Oerum, S, Rossmanith, W, Yue, WW, Zschocke, J, Munro, KJ, Battersby, BJ, Friedman, TB, Taylor, RW, O'Keefe, RT and Newman, WG.

    Bi-allelic variants in the mitochondrial RNase P subunit PRORP cause mitochondrial tRNA processing defects and pleiotropic multisystem presentations

    American Journal of Human Genetics 108(11): 2195-2204

    [doi:10.1016/j.ajhg.2021.10.002]

  • Quijada-Fraile, P, Canales, EA, Martin-Hernandez, E, Ballesta-Martinez, MJ, Guillen-Navarro, E, Pintos-Morell, G, Molto-Abad, M, Moreno-Martinez, D, Morillo, SG, Blasco-Alonso, J, Couce, ML, Sanchez, RG, Cortes-Saladelafont, E, Rodriguez, MAL, Garcia-Silva, MT and Conejo, MM.

    Clinical features and health-related quality of life in adult patients with mucopolysaccharidosis IVA: the Spanish experience

    Orphanet Journal of Rare Diseases 16(1): 464-464

    [doi:10.1186/s13023-021-02074-y]

  • Sune, CH, Lopez, CC, Lopez, PM, Senosiain, OG, Escribano, MD, Poyatos, JV, Barcelo, LH, Alcazar, AR, Carrera-Burgaya, A, De la Torre, FR, Martinez-Pineiro, A and Cabezas, EA.

    The sternohyoid muscle flap for new dynamic facial reanimation technique: Anatomical study and clinical results

    JOURNAL OF PLASTIC RECONSTRUCTIVE AND AESTHETIC SURGERY 74(11): 3040-3047

    [doi:10.1016/j.bjps.2021.03.085]

  • Lucente, G, Corral, J, Rodriguez-Esparragoza, L, Castaner, S, Ortiz, H, Piqueras, A, Broto, J, Hernandez-Perez, M, Domenech, S, Martinez-Pineiro, A, Serra, J, Almendrote, M, Pares, D and Millan, M.

    Current Incidence and Risk Factors of Fecal Incontinence After Acute Stroke Affecting Functionally Independent People

    Frontiers in Neurology 12: 755432-755432

    [doi:10.3389/fneur.2021.755432]

  • Keller, M, Brennenstuhl, H, Hubschmann, OK, Manti, F, Palacios, NAJ, Friedman, J, Yildiz, Y, Koht, JA, Wong, SN, Zafeiriou, DI, Lopez-Laso, E, Pons, R, Kulhanek, J, Jeltsch, K, Serrano-Lomelin, J, Garbade, SF, Opladen, T, Goez, H, Burlina, A, Cortes-Saladelafont, E, Ramos, JAF, Garcia-Cazorla, A, Hoffmann, GF, Hong, STK, Honzik, T, Kavecan, I, Kurian, MA, Leuzzi, V, Lucke, T, Manzoni, F, Mastrangelo, M, Mercimek-Andrews, S, Mir, P, Oppeboen, M, Pearson, TS, Sivri, HS, Steel, D, Stevanovic, G and Fung, CW.

    Assessment of intellectual impairment, health-related quality of life, and behavioral phenotype in patients with neurotransmitter related disorders: Data from the iNTD registry

    Journal of Inherited Metabolic Disease 44(6): 1489-1502

    [doi:10.1002/jimd.12416]

  • Salazar-Martinez, E, Santalla, A, Valenzuela, PL, Nogales-Gadea, G, Pinos, T, Moran, M, Santos-Lozano, A, Fiuza-Luces, C and Lucia, A.

    The Second Wind in McArdle Patients: Fitness Matters

    Frontiers in Physiology 12: 744632-744632

    [doi:10.3389/fphys.2021.744632]

  • Hubschmann, OK, Horvath, G, Cortes-Saladelafont, E, Yildiz, Y, Mastrangelo, M, Pons, R, Friedman, J, Mercimek-Andrews, S, Wong, SN, Pearson, TS, Zafeiriou, DI, Kulhanek, J, Kurian, MA, Lopez-Laso, E, Oppeboen, M, Kilavuz, S, Wassenberg, T, Goez, H, Scholl-Burgi, S, Porta, F, Honzik, T, Santer, R, Burlina, A, Sivri, HS, Leuzzi, V, Hoffmann, GF, Jeltsch, K, Hubschmann, D, Garbade, SF, Garcia-Cazorla, A and Opladen, T.

    Insights into the expanding phenotypic spectrum of inherited disorders of biogenic amines

    Nature Communications 12(1): 5529-5529

    [doi:10.1038/s41467-021-25515-5]

  • Verdura, E, Rodriguez-Palmero, A, Velez-Santamaria, V, Planas-Serra, L, de la Calle, I, Raspall-Chaure, M, Roubertie, A, Benkirane, M, Saettini, F, Pavinato, L, Mandrile, G, O'Leary, M, O'Heir, E, Barredo, E, Chacon, A, Michaud, V, Goizet, C, Ruiz, M, Schluter, A, Rouvet, I, Sala-Coromina, J, Fossati, C, Iascone, M, Canonico, F, Marce-Grau, A, de Souza, P, Adams, DR, Casasnovas, C, Rehm, HL, Mefford, HC, Gutierrez-Solana, LG, Brusco, A, Koenig, M, Macaya, A and Pujol, A.

    Biallelic PI4KA variants cause a novel neurodevelopmental syndrome with hypomyelinating leukodystrophy

    Brain 144(9): 2659-2669

    [doi:10.1093/brain/awab124]

  • Hubschmann, OK, Mohr, A, Friedman, J, Manti, F, Horvath, G, Cortes-Saladelafont, E, Mercimek-Andrews, S, Yildiz, Y, Pons, R, Kulhanek, J, Oppeboen, M, Koht, JA, Podzamczer-Valls, I, Domingo-Jimenez, R, Ibanez, S, Alcoverro-Fortuny, O, Gomez-Alemany, T, de Castro, P, Alfonsi, C, Zafeiriou, DI, Lopez-Laso, E, Guder, P, Santer, R, Honzik, T, Hoffmann, GF, Garbade, SF, Sivri, HS, Leuzzi, V, Jeltsch, K, Garcia-Cazorla, A, Opladen, T and Harting, I.

    Brain MR patterns in inherited disorders of monoamine neurotransmitters: An analysis of 70 patients

    Journal of Inherited Metabolic Disease 44(4): 1070-1082

    [doi:10.1002/jimd.12360]

  • Alvarez-Velasco, R, Gutierrez-Gutierrez, G, Trujillo, JC, Martinez, E, Segovia, S, Arribas-Velasco, M, Fernandez, G, Paradas, C, Velez-Gomez, B, Casasnovas, C, Nedkova, V, Guerrero-Sola, A, Ramos-Fransi, A, Martinez-Pineiro, A, Pardo, J, Sevilla, T, Gomez-Caravaca, MT, de Munain, AL, Jerico, I, Pelayo-Negro, AL, Martin, MA, Morgado, Y, Mendoza, MD, Perez-Perez, H, Rojas-Garcia, R, Turon-Sans, J, Querol, L, Gallardo, E, Illa, I and Cortes-Vicente, E.

    Clinical characteristics and outcomes of thymoma-associated myasthenia gravis

    European Journal of Neurology 28(6): 2083-2091

    [doi:10.1111/ene.14820]

  • Lucente G, Martinez-Barenys C, Ramos-Fransi A, Almendrote-Muñoz M, López de Castro P, Deletis V, Coll-Canti J and Martínez-Piñeiro A.

    A New Methodology for Intraoperative Monitoring of the Functional Integrity of the Phrenic Nerve During Cardiothoracic Surgery.

    Journal of Clinical Neurophysiology 38(3): 226-230

    [doi:10.1097/WNP.0000000000000677]

  • Rodriguez-Palmero, A, Boerrigter, MM, Gomez-Andres, D, Aldinger, KA, Marcos-Alcalde, I, Popp, B, Everman, DB, Lovgren, AK, Arpin, S, Bahrambeigi, V, Beunders, G, Bisgaard, AM, Bjerregaard, VA, Bruel, AL, Challman, TD, Cogne, B, Coubes, C, de Man, SA, Denomme-Pichon, AS, Dye, TJ, Elmslie, F, Feuk, L, Garcia-Minaur, S, Gertler, T, Giorgio, E, Gruchy, N, Haack, TB, Haldeman-Englert, CR, Haukanes, BI, Hoyer, J, Hurst, ACE, Isidor, B, Soller, MJ, Kushary, S, Kvarnung, M, Landau, YE, Leppig, KA, Lindstrand, A, Kleinendorst, L, MacKenzie, A, Mandrile, G, Mendelsohn, BA, Moghadasi, S, Morton, JE, Moutton, S, Muuller, AJ, O'Leary, M, Pacio-Miguez, M, Palomares-Bralo, M, Parikh, S, Pfundt, R, Pode-Shakked, B, Rauch, A, Repnikova, E, Revah-Politi, A, Ross, MJ, Ruivenkamp, CAL, Sarrazin, E, Savatt, JM, Schluter, A, Schonewolf-Greulich, B, Shad, Z, Shaw-Smith, C, Shieh, JT, Shohat, M, Spranger, S, Thiese, H, Mau-Them, FT, van Bon, B, van de Burgt, I, van de Laar, IMBH, van Drie, E, van Haelst, MM, van Ravenswaaij-Arts, CM, Verdura, E, Vitobello, A, Waldmuller, S, Whiting, S, Zweier, C, Prada, CE, de Vries, BBA, Dobyns, WB, Reiter, SF, Gomez-Puertas, P, Pujol, A and Tumer, Z.

    DLG4-related synaptopathy: a new rare brain disorder

    Genetics in Medicine 23(5): 888-899

    [doi:10.1038/s41436-020-01075-9]

  • de Moura, MC, Davalos, V, Planas-Serra, L, Alvarez-Errico, D, Arribas, C, Ruiz, M, Aguilera-Albesa, S, Troya, J, Valencia-Ramos, J, Velez-Santamaria, V, Rodriguez-Palmero, A, Villar-Garcia, J, Horcajada, JP, Albu, S, Casasnovas, C, Rull, A, Reverte, L, Dietl, B, Dalmau, D, Arranz, MJ, Llucia-Carol, L, Planas, AM, Perez-Tur, J, Fernandez-Cadenas, I, Villares, P, Tenorio, J, Colobran, R, Martin-Nalda, A, Soler-Palacin, P, Vidal, F, Pujol, A and Esteller, M.

    Epigenome-wide association study of COVID-19 severity with respiratory failure

    EBioMedicine 66: 103339-103339

    [doi:10.1016/j.ebiom.2021.103339]

  • Hurtado, E, Nunez-Alvarez, Y, Munoz, M, Gutierrez-Caballero, C, Casas, J, Pendas, AM, Peinado, MA and Suelves, M.

    HDAC11 is a novel regulator of fatty acid oxidative metabolism in skeletal muscle

    FEBS Journal 288(3): 902-919

    [doi:10.1111/febs.15456]

  • Nunez-Alvarez, Y, Hurtado, E, Munoz, M, Garcia-Tunon, I, Rech, GE, Pluvinet, R, Sumoy, L, Pendas, AM, Peinado, MA and Suelves, M.

    Loss of HDAC11 accelerates skeletal muscle regeneration

    FEBS Journal 288(4): 1201-1223

    [doi:10.1111/febs.15468]

  • Alvarez, M, Lucente, G, Martinez, L, Almendrote, M, Ramos, A, Broto, J, Arbex, A, Coll, J, Sancho, J and Martinez, A.

    Paraplegia Following Type B Acute Aortic Dissection Can Spare the Spinal Cord

    Annals of Vascular Surgery 70:

    [doi:10.1016/j.avsg.2020.08.133]

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